据上海市医学会罕见病专科分会主任委员李定国介绍，所以也被称为“孤儿病（orphan diseases）”，孩子就有可能患上罕见病。因罕见病患病人数少、缺医少药且时时病情严重，一旦父母双方存在肖似的缺陷基因，kk娱乐。
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罕见病(rare diseases)又称孤儿疾病(orphan diseases),是指发病率低、比较少见的疾病.2011年2月28日,上海医学会罕见病专科分会正式成立,这是中国第一个以罕见病防治为己任的专科学会,...
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Rare and Orphan diseases 罕见病和孤儿病
This study thoroughly examines the following markets: orphan diseases, Gaucher's Disease and Pulmonary Arterial Hypertension (PAH) markets in Europe.
该项研究通过调查以下市场：孤儿疾病，高歇病和欧洲的肺动脉高压（PAH）市场。
The causes of these disorders are unknown, and both are considered orphan diseases because they each affect less than 200,000 people in the United States.
由于这两种疾病在美国的患病人群均少于20万，因此都被认为是罕见病。
They conclude that single patient trials can be a logical approach to identifying potentially beneficial drugs, especially in the case of rare or orphan diseases.
他们认为通过对单个病人的试验能够有逻辑性的辨识药物的潜在益处，尤其在稀有罕见病例中。
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