The ultimate goal of gene therapy is correction of the genetic disorders by introducing the genetic materials into targeted cells, and gene expression should be permanent and at an appropriate level.
基因治疗的目的是将遗传物质导入细胞并使之得到适宜水平的表达，以纠正机体的遗传缺陷，恢复细胞的正常功能或杀死癌细胞及致病微生物。
Targeted gene expression to the epidermis has been achieved, but was neither a prerequisite for correction nor did it improve longevity of expression.
皮肤靶向基因的表达已完成测序，但这并不是我们就能对它进行修饰的先决条件。
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