BACKGROUND Increasing the activity of defective cystic fibrosis transmembrane conductance regulator (CFTR) protein is a potential treatment for cystic fibrosis.

背景提高有缺陷的囊性纤维化跨膜电导调节(CFTR)蛋白的活性是囊性纤维化的一种潜在治疗。

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The idea is this: Kalydeco works by improving the function of the Cystic Fibrosis Transmembrane Regulator protein.

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Kalydeco works by correcting the protein that is defective in cystic fibrosis, called the cystic fibrosis transmembrane conductance regulator, which helps move salt ions across cells.

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