Objective To make a correct diagnosis in the early stage and avoid misdiagnosis, we analysed clinical data of patients with Duchenne type muscular dystrophy(DMD).

目的通过对进行性肌营养不良的临床综合分析，探讨该病的早期诊断方法，减少误诊。

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One big question: would the limited data Sarepta has so far collected from a very small clinical trial of its drug eteplirsen, a treatment for Duchenne muscular dystrophy that is caused by a very specific type of mutation, be enough to warrant filing with the Food and Drug Administration and perhaps even gain approval?

FORBES: A Key Exchange On Sarepta Therapeutics' Promising Muscular Dystrophy Drug