·腺嘌呤去胺酶缺乏症(Adenosine deaminase deficiency , ADA deficiency) 是一种罕见的免疫不全症。罹病的原因是一种称为腺嘌呤去胺酶缺陷所导致。
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The Glaxo gene therapy program will focus on a severe immune deficiency called ADA-SCID, in which kids cannot make a crucial enzyme called adenosine deaminase that is needed to create immune system cells.
FORBES: Glaxo Brings Gene Therapy Back From The Dead
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