No dear,Nature made you so perfectly that this small defect shocks me as being a sign of earthly imperfection."

VOA: special.2009.09.26

Usually this is a disease that's caused by a defect in a single gene.

通常在疾病是由,单基因缺陷引起时才可行

耶鲁公开课 - 生物医学工程探索课程节选

Because of this, because cystic fibrosis is a disease that's caused by a single gene defect, there's been great interest in trying to treat cystic fibrosis with gene therapy.

就是因为如此,就因为囊胞性纤维症,是一种单基因病,人们对于用基因治疗,治愈囊胞性纤维症产生了很大的兴趣

耶鲁公开课 - 生物医学工程探索课程节选