He speculates that it could also cut the disease's rate of progression in half, extending life by as much as a decade and being a necessary treatment for anyone at risk for the disease.

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Nine children showed greater than a 50% increase in annual rate of weight gain, a statistically significant result, but six children lost weight, perhaps because of disease progression or side effects of the medicine.

WSJ: Progeria Drug Study Helps in Search for Clues on Aging

Celldex CEO Anthony Marucci has said previously that a meaningful and positive response rate in the study would be 12% to 15% with a progression-free survival of greater than 12 weeks.

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