In late 2001, Gage called Valerie Estess, the research head for Project ALS, and explained the idea.

FORBES: Gene Therapy Slows A Killer

In an earlier result, Project ALS researchers discovered that the arthritis drug Celebrex may help slow the progression of the disease.

FORBES: Gene Therapy Slows A Killer

After quickly consulting Project ALS scientific advisors, who also were gung-ho, she cut a check to get the research started within days.

FORBES: Gene Therapy Slows A Killer

Project ALS is now negotiating with government regulators and undisclosed biotech firms to design a human trial that could begin next year.

FORBES: Gene Therapy Slows A Killer

The gene therapy experiment was largely funded by Project ALS, an innovative charity founded by ALS-sufferer Jenifer Estess and two of her sisters.

FORBES: Gene Therapy Slows A Killer

Project ALS originally funded Dr. Gage several years ago in hopes of developing stem cell treatments for ALS, work that is still ongoing.

FORBES: Gene Therapy Slows A Killer

The Project ALS success could also give a big boost to the gene therapy field, which has fallen on hard times after numerous gene therapy treatments proved ineffective or caused serious side effects.

FORBES: Gene Therapy Slows A Killer