A rare disease, also referred to as an orphan disease, is any disease that affects a small percentage of the population.
罕见病，也被称为孤儿病，指那些仅在极少数人群身上发生的疾病。
Pigmented Villonodular Synovitis is a benign orphan disease with trend of local infiltration. Its clinical manifestation is atypical.
色素沉着绒毛结节性滑膜炎是一种良性的，但具有局部浸润倾向的罕见疾病，临床症状不典型。
This study thoroughly examines the following markets: orphan diseases, Gaucher's Disease and Pulmonary Arterial Hypertension (PAH) markets in Europe.
该项研究通过调查以下市场：孤儿疾病，高歇病和欧洲的肺动脉高压（PAH）市场。
Orphan drug designation is available for drugs already approved for another disease or condition or for experimental drugs that have not been previously approved.
已经被批准用于其它疾病治疗的药物或者是尚处于试验阶段未被批准的药物都可以通过孤儿药物申报程序进行。
To obtain orphan drug designation, drugs must be for the treatment, prevention or diagnosis of a rare disease or condition.
孤儿药物审批流程需要该药物可以用于治疗、预防或者诊断罕见疾病。
Orphan drug status provides the company with financial incentives to promote the development of a drug to treat a rare disease or condition.
稀少药品状态提供给药品公司金融鼓励，促使药品公司开发治疗稀少疾病的药物。
During the workshop, participants will propose a specific drug for a specific rare disease and work on an orphan designation application to submit to the FDA at the conclusion of the workshop.
研讨会期间，与会者将提出一个具体的孤儿药物按照FDA的孤儿药物审批过程进行研讨，并将其申请提交给FDA作为研讨会的总结。
PURPOSE of review: The present review highlights an orphan infectious disease in alarming need of international recognition.
综述目的：本综述阐述一个亟需全世界认识的小儿感染性疾病。
PURPOSE of review: The present review highlights an orphan infectious disease in alarming need of international recognition.
综述目的：本综述阐述一个亟需全世界认识的小儿感染性疾病。
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